Future Therapy for Pediatric Hereditary Angioedema
نویسنده
چکیده
Hereditary angioedema (HAE) due to C1-inhibitor (C1-INH) deficiency is characterized by recurrent attacks of swelling with symptoms typically beginning in childhood. The introduction of targeted therapies for prevention and treatment of attacks has been of significant benefit to patients, including children, with HAE. However, the ideal of a safe, convenient therapy that prevents all attacks has not been realized. New approaches including ongoing inhibition of plasma kallikrein, and perhaps activated Factor XII, show promise in further improving the care of patients with HAE.
منابع مشابه
Hereditary Angioedema: Moving Therapy into the Home and to Self-Care
Hereditary angioedema (HAE) is a condition that results in recurrent and often unpredictable attacks of angioedema, which is associated with significant morbidity and can be fatal. The majority of literature related to management of HAE has focused on the adult patient. There is limited information on treatment and management strategies for the pediatric HAE population. Comprehensive care has b...
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